authors Herdt, Aimee R Peng, Hui Dickson, Dennis W Todd Golde, MD, PhD Eckman, Elizabeth A Lee, Chris W
has subject area Animals Body Weight Galactosylceramidase Hydrolases Leukodystrophy, Globoid Cell Longevity Mice Prosencephalon Psychosine White Matter
Keywords Krabbe disease adeno-associated virus serotype 1 galactosylceramidase gene therapy psychosine twitcher