Skeletal muscle effects of antisense oligonucleotides targeting glycogen synthase 1 in a mouse model of Pompe disease. uri icon

authors

  • Weiss, Lan
  • Fazeli, Yasamin
  • Chang, Mindy
  • Paguio, Marvin
  • Lee, Jonathan
  • Yu, Howard
  • Weiss, John
  • Grossman, Tamar R
  • Raben, Nina
  • Jafar-Nejad, Paymaan
  • Kimonis, Virginia
  • Carrer, Michele
  • Shmara, Alyaa
  • Martin, Angela
  • Yin, Hong
  • Pal, Pallabi
  • Cheng, Cheng
  • Ta, Lac
  • Boock, Victoria

publication date

  • April 2025