Elucidating brain transport pathways and cell type-dependent gene silencing of a durable lipid-siRNA conjugate administered into cerebrospinal fluid. uri icon

authors

  • Sorets, Alexander G
  • Park, Joshua C
  • Ligocki, Alexander P
  • Ford, William T
  • Ventura-Antunes, Lissa
  • Hoogenboezem, Ella N
  • Prusky, Alex
  • Castleberry, Mark
  • Michell, Danielle L
  • Fritsch, Emma
  • Lyons, Sarah M
  • Schwensen, Katrina R
  • Miller, Timothy M
  • Vickers, Kasey C
  • Schrag, Matthew S
  • Duvall, Craig L
  • Lippmann, Ethan S
  • Francini, Nora
  • Kjar, Andrew
  • Abdulrahman, Adam M
  • Shostak, Alena
  • Katdare, Ketaki A
  • Schoch, Kathleen M
  • Cowell, Rebecca P

publication date

  • June 20, 2025