Patient-Reported Meaningful Change in Symptoms and Impacts of Paroxysmal Nocturnal Hemoglobinuria (PNH) in Three Phase III Clinical Trials of Iptacopan. uri icon

authors

  • DeCastro, Carlos
  • Lamoureux, Roger
  • Rupinski, Kaelyn
  • Lowe, Caitlyn
  • Nieves, Amber
  • de Fontbrune, Flore Sicre
  • de Latour, Regis Peffault
  • Sheinberg, Phillip
  • Han, Bing
  • Vallow, Susan
  • Bermann, Georgina
  • Dhalke, Marion
  • Kumar, Rakesh
  • Dickie, Gavin
  • Galipeau, Nina

publication date

  • July 22, 2025